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Acid Sphingomyelinase Deficiency Questions

Related terms: ASMD, Sphingolipidosis

Displaying 2 questions associated with Acid Sphingomyelinase Deficiency.

How effective is Xenpozyme?

How quickly does Xenpozyme (olipudase alfa-rpcp) work?

How does Xenpozyme work?

Does Xenpozyme cure acid sphingomyelinase deficiency (ASMD)?

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