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Acid Sphingomyelinase Deficiency News
Related terms: ASMD, Sphingolipidosis
FDA Approves Xenpozyme (olipudase alfa-rpcp) for Non-CNS Manifestations of Acid Sphingomyelinase Deficiency (ASMD)
Paris, August 31, 2022 – The U.S. Food and Drug Administration (FDA) has approved Xenpozyme (olipudase alfa-rpcp) for the treatment of non-central nervous system (non-CNS) manifestations of acid...
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